Rare Disease Innovation& Partnering Summit

Generate solution-focused strategies surrounding patient access, reimbursement, commercialization, launch, partnering and more. Join experts from across the rare disease community to unite in areas of unmet medical need and create life-transforming therapies and breakthroughs. 

SEE WHAT ATTENDEES EXPERIENCED IN 2022:

Have a topic in mind for the 2023 agenda? Let us know! 

Novel Approaches to High-Impact Topics:

• Strengthen Patient Relationships Authentically to Enhance the Therapeutic Development Process
• Foster Effective Relationships Between Industry and Advocacy
• Leverage Genetic Testing for Value for Rare Disease Patients
• Reflect on the Impact of Covid-19 on the Rare Disease Community
• Identify Gaps and Develop Solutions to Promote Diversity, Equity and Inclusion
• Optimize Decentralized Trials to Support the Future of Rare Disease Research

A Custom Learning Experience:

Customize your agenda with focused breakouts including topic areas on:

• Patient-Driven Progress - Driving models to advancing company formation, advocacy and drug development le by patients and disease foundations
• Reimbursement, Value and Access - Evolving pricing, value-based payment and reimbursement trends impacting market and patient access to orphan products
• New Launch and Commercialization - Critical strategies and commercialization frameworks for launching products within the rare disease market
• Partnering, Investment and Portfolio Strategy - Opportunities for collaboration, value growth drivers and funding inflection points to propel innovation

Paving the Way - Your Expert Speakers:

• Alexion Pharmaceuticals
• Angelman Syndrome Foundation
• Apellis Pharmaceuticals
• bluebird bio
• Cognito Therapeutics
• CureCMT4J
• Cydan
• DDX3X Foundation
• FDA/CDER/OND/ORDPURM
• NS Pharma
• Rafael Pharmaceuticals
• Sanofi
• TargetCancer Foundation
• Tremeau Pharmaceuticals

THANK YOU TO OUR 2022 SPEAKING FACULTY!

Want to speak at our 2023 event, or do you have a fabulous speaker in mind? Let us know!

WHO SHOULD ATTEND

You will benefit from attending this event if you work for a company that focuses on rare disease and orphan drugs and have responsibilities or involvement in the following areas:

Market Access

Rare Disease

Orphan Drugs

Commercial Strategy/Operations

Reimbursement

Early/Expanded Access

Launch Excellence

Product Launch

Portfolio Management/Strategy

Marketing

Development

Patient Advocacy

Payer Strategy

Patient Support/Services

This event will also benefit consultants and solution providers who provide services in the rare disease space.

CONNECT AND NETWORK WITH KEY DECISION-MAKERS AT THE RARE DISEASE SUMMIT

Whether you’re looking to generate quality leads, showcase thought leaders, or reinforce your brand, collaborate with us to identify custom sponsorship opportunities to help you reach your business objectives.

For more information about custom opportunities to reach a qualified audience, please contact us here.

l thought this was one of the best conferences I've attended overthe years.The focus was very practical and each speaker sharedreal world examples instead of theory.It was well organized andthe passion each participant has for helping people with raredisease was very evident.

The Rare Disease lnnovation Summit provided the opportunity forcross communication between industry, nonprofits and vendorswho bridge the gap between the two.From presentations topanels, every attendee walked away with new information andresources to help improve the quality of life for the rare diseasecommunity.Thank you for making this possible CBI!

The inaugural Rare Disease Innovation Conference broughttogether multidisciplinary stakeholders to discuss importantissues challenging the rare disease ecosystem.The contributionsby the audience accelerated thinking how to address and

eventually resolve key access related issues impacting people indesperate need of therapeutic options.

Most amazing were the voices from the patient community whoare driving drug discovery and access. What some doing for a fewbenefits us all in this rare space.CBI's Summit was a prime

example of how the patients are critical to informing the researchand development dialogue but also vice versa. We need to knowthe innovations planned and in progress.

The rare Innovation summit is an intimate engaging meeting

facilitating discussion amongst speakers and attendees - nice mixof industry and patient groups especially stakeholders l haven'tmet before at other meetings.

Browse the Full 2022 Brochure